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Öğe Emapalumab treatment in an ADA-SCID patient with refractory hemophagocytic lymphohistiocytosis-related graft failure and disseminated bacillus Calmette-Guerin infection(Ferrata Storti Foundation, 2021) Tucci, Francesca; Gallo, Vera; Barzaghi, Federica; Ferrua, Francesca; Migliavacca, Maddalena; Calbi, Valeria; Doglio, Matteo[Abstract Not Availabe]Öğe Gene Therapy for Adenosine Deaminase Deficiency: Long-Term Outcome and Post-Marketing Experience(Cell Press, 2023) Migliavacca, Maddalena; Barzaghi, Federica; Fossati, Claudia; Rancoita, Paola M. V.; Gabaldo, Michela; Dionisio, Francesca; Giannelli, Stefania[Abstract Not Availabe]